ABCD4

UniProt ID: O14678
Organism: Homo sapiens
Review Status: INITIALIZED
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Gene Description

ABCD4 (cblJ complementation group; formerly PMP69/P70R/PXMP1-L) is a half-size ATP-binding cassette (ABC) transporter of subfamily D that exports cobalamin (vitamin B12) from the lysosomal lumen to the cytosol in an ATP-dependent manner. Unlike its peroxisomal paralogs ABCD1-ABCD3, ABCD4 lacks the N-terminal hydrophilic region associated with peroxisomal targeting; it is co-translationally inserted into the endoplasmic reticulum membrane and requires the lysosomal escort protein LMBD1 (LMBRD1) to translocate to and localize at the lysosomal membrane, where it functions as a homodimer. After transcobalamin-bound cobalamin is endocytosed and degraded in the lysosome, ABCD4 (in concert with LMBD1 and the cytosolic processing protein MMACHC) delivers free cobalamin to the cytosol for conversion to methylcobalamin and adenosylcobalamin, the cofactors of methionine synthase and methylmalonyl-CoA mutase. Loss-of-function mutations cause methylmalonic aciduria and homocystinuria type cblJ (MAHCJ), characterized by failure to release cobalamin from lysosomes and reduced levels of both cobalamin cofactors.

Existing Annotations Review

GO Term Evidence Action Reason
GO:0005778 peroxisomal membrane
IBA
GO_REF:0000033
REMOVE
Summary: Human ABCD4 follows an ER-to-lysosome targeting route and was experimentally excluded from peroxisomes.
Reason: PTHR11384 places the peroxisomal-membrane IBD at PTN004256010. Target-specific localization and targeting experiments, rather than donor number or absent fatty-acid assays, challenge inheritance of that compartment in ABCD4. PMID:19010322 reports full-length P70R-HA in the ER rather than peroxisomes and identifies its divergent N-terminal targeting architecture; PMID:27456980 establishes endogenous ER/lysosome localization and LMBD1-dependent lysosomal delivery. These findings support rejecting native peroxisomal-membrane localization while preserving the two experimental NOT annotations.
Propagation Review
Root cause: PROPAGATION BAD
Failure modes: COMPARTMENT OR COMPLEX MISMATCH
Sources checked:
PANTHER:PTN004256010 · PTN004256010 SUPPORTS SOURCE BUT NOT TARGET
The ancestral peroxisomal ABC transporter node is challenged by direct ABCD4 localization and targeting divergence.
Supporting Evidence:
PMID:27456980
ABCD4 does not localize to peroxisomes
PMID:19010322
only P70R lacks the region and is translated with NH(2)-terminal hydrophobic TMS1.
GO:0042626 ATPase-coupled transmembrane transporter activity
IBA
GO_REF:0000033
ACCEPT
Summary: ATPase-coupled transmembrane transporter activity accurately describes the membrane-embedded ABCD4 cobalamin transporter.
Reason: Purified ABCD4 reconstituted in liposomes catalyzes ATP-dependent cobalamin translocation (PMID:33845046); localization experiments establish ER and lysosomal membranes (PMID:27456980). The broad transporter, transport and membrane terms are true core properties alongside the more specific vitamin-B12 transporter annotation. Greater specificity does not make these existing parent-level assertions over-annotations.
Propagation Review
Root cause: NO FAILURE CORE
Sources checked:
PANTHER:PTN004256010 · PTN004256010 SUPPORTS TRANSFER
ABCD4 retains the ABC ATPase-coupled transport mechanism despite substrate and compartment divergence.
Supporting Evidence:
PMID:33845046
ABCD4 transports cobalamin from the inside to the outside of liposomes in a manner that is dependent on ATPase activity
GO:0005324 long-chain fatty acid transmembrane transporter activity
IBA
GO_REF:0000033
UNDECIDED
Summary: The inherited long-chain fatty acid transmembrane transporter activity assertion needs assessment independently of ABCD4 cobalamin transport and peroxisome exclusion.
Reason: The relevant IBD is at PTN004256010 in PTHR11384. Direct B12 transport establishes one substrate, but is not a negative assay for every fatty-acid transport activity. Likewise, an ER/lysosomal protein can in principle affect peroxisome organization or lipid metabolism without being a peroxisomal resident. The previous removal conflated these distinct claims. Retain uncertainty pending focused evaluation of ancestral process evidence, target-specific substrate tests and pathway participation.
Propagation Review
Root cause: UNRESOLVED
Sources checked:
PANTHER:PTN004256010 · PTN004256010 UNRESOLVED
The node asserts this function; B12 specificity and negative peroxisome localization do not independently adjudicate this separate activity/process.
GO:0006635 fatty acid beta-oxidation
IBA
GO_REF:0000033
UNDECIDED
Summary: The inherited fatty acid beta-oxidation assertion needs assessment independently of ABCD4 cobalamin transport and peroxisome exclusion.
Reason: The relevant IBD is at PTN004256010 in PTHR11384. Direct B12 transport establishes one substrate, but is not a negative assay for every fatty-acid transport activity. Likewise, an ER/lysosomal protein can in principle affect peroxisome organization or lipid metabolism without being a peroxisomal resident. The previous removal conflated these distinct claims. Retain uncertainty pending focused evaluation of ancestral process evidence, target-specific substrate tests and pathway participation.
Propagation Review
Root cause: UNRESOLVED
Sources checked:
PANTHER:PTN004256010 · PTN004256010 UNRESOLVED
The node asserts this function; B12 specificity and negative peroxisome localization do not independently adjudicate this separate activity/process.
GO:0015910 long-chain fatty acid import into peroxisome
IBA
GO_REF:0000033
REMOVE
Summary: ABCD4 does not support the assigned role of importing long-chain fatty acids across the peroxisomal membrane.
Reason: This is a compartment-specific transport claim placed at PTN004256010. Direct ABCD4 targeting/localization experiments show an ER-to-lysosome itinerary and exclude the peroxisomal membrane in the studied context. That target-specific compartment divergence challenges peroxisomal import, independently of whether ABCD4 has any untested fatty-acid transport capacity in other membranes. Do not generalize this rejection into proof of absent fatty-acid chemistry.
Propagation Review
Root cause: PROPAGATION BAD
Failure modes: COMPARTMENT OR COMPLEX MISMATCH
Sources checked:
PANTHER:PTN004256010 · PTN004256010 SUPPORTS SOURCE BUT NOT TARGET
ABCD4 diverged in targeting from the ancestral peroxisomal transporter context.
Supporting Evidence:
PMID:27456980
ABCD4 does not localize to peroxisomes
PMID:19010322
only P70R lacks the region and is translated with NH(2)-terminal hydrophobic TMS1.
GO:0042760 very long-chain fatty acid catabolic process
IBA
GO_REF:0000033
UNDECIDED
Summary: The inherited very long-chain fatty acid catabolic process assertion needs assessment independently of ABCD4 cobalamin transport and peroxisome exclusion.
Reason: The relevant IBD is at PTN004256010 in PTHR11384. Direct B12 transport establishes one substrate, but is not a negative assay for every fatty-acid transport activity. Likewise, an ER/lysosomal protein can in principle affect peroxisome organization or lipid metabolism without being a peroxisomal resident. The previous removal conflated these distinct claims. Retain uncertainty pending focused evaluation of ancestral process evidence, target-specific substrate tests and pathway participation.
Propagation Review
Root cause: UNRESOLVED
Sources checked:
PANTHER:PTN004256010 · PTN004256010 UNRESOLVED
The node asserts this function; B12 specificity and negative peroxisome localization do not independently adjudicate this separate activity/process.
GO:0005524 ATP binding
IBA
GO_REF:0000033
ACCEPT
Summary: ATP binding by the nucleotide-binding domain, inferred phylogenetically and consistent with the Walker A/B motifs and demonstrated ATPase-dependent transport.
Reason: ABCD4 contains a canonical ABC nucleotide-binding domain (Walker A motif, residues 421-428) and its transport activity is ATP-hydrolysis-dependent (K427A Walker A mutant abolishes activity), so ATP binding is well supported.
Supporting Evidence:
PMID:33845046
ABCD4 (K427A) had lost transport activity in addition to ATPase activity
GO:0007031 peroxisome organization
IBA
GO_REF:0000033
UNDECIDED
Summary: The inherited peroxisome organization assertion needs assessment independently of ABCD4 cobalamin transport and peroxisome exclusion.
Reason: The relevant IBD is at PTN004256010 in PTHR11384. Direct B12 transport establishes one substrate, but is not a negative assay for every fatty-acid transport activity. Likewise, an ER/lysosomal protein can in principle affect peroxisome organization or lipid metabolism without being a peroxisomal resident. The previous removal conflated these distinct claims. Retain uncertainty pending focused evaluation of ancestral process evidence, target-specific substrate tests and pathway participation.
Propagation Review
Root cause: UNRESOLVED
Sources checked:
PANTHER:PTN004256010 · PTN004256010 UNRESOLVED
The node asserts this function; B12 specificity and negative peroxisome localization do not independently adjudicate this separate activity/process.
GO:0005524 ATP binding
IEA
GO_REF:0000002
ACCEPT
Summary: InterPro-based ATP binding from the ABC transporter ATP-binding domain signatures. Consistent with the experimentally supported nucleotide-binding domain.
Reason: The InterPro domain signatures (ABC transporter-like ATP-binding domain) correctly identify the nucleotide-binding domain; ATP binding is supported by the Walker A motif and ATPase-dependent transport.
Supporting Evidence:
PMID:33845046
ABCD4 (K427A) had lost transport activity in addition to ATPase activity
GO:0005765 lysosomal membrane
IEA
GO_REF:0000044
ACCEPT
Summary: UniProt Subcellular Location mapping to the lysosomal membrane, corroborated by multiple experimental studies.
Reason: The lysosomal membrane is the functional location of ABCD4, established experimentally; the SubCell IEA is consistent with the direct evidence.
Supporting Evidence:
file:human/ABCD4/ABCD4-uniprot.txt
Lysosome membrane {ECO
PMID:22922874
in failure to release vitamin B12 from lysosomes, which mimics the cblF defect
GO:0005789 endoplasmic reticulum membrane
IEA
GO_REF:0000120
ACCEPT
Summary: Automated (multi-method) mapping to the ER membrane. ABCD4 is co-translationally inserted into the ER before LMBD1-dependent translocation to lysosomes, so ER membrane is a genuine (biosynthetic-intermediate) location.
Reason: Experimental studies show endogenous ABCD4 resides in both the ER and lysosomal membranes, the ER being the site of synthesis/insertion prior to LMBD1-mediated lysosomal targeting.
Supporting Evidence:
PMID:27456980
ABCD4 was not a peroxisomal protein, but rather, an ER protein
PMID:19010322
P70R-HA was localized to the endoplasmic
GO:0015420 ABC-type vitamin B12 transporter activity
IEA
GO_REF:0000003
ACCEPT
Summary: EC 7.6.2.8 (ABC-type vitamin B12 transporter) mapped to the specific GO molecular function. This matches the experimentally demonstrated cobalamin transport activity of ABCD4.
Reason: This is the core molecular function of ABCD4, independently supported by direct in vitro transport assays. The EC-to-GO mapping is correct.
Supporting Evidence:
PMID:33845046
ABCD4 transports cobalamin from the inside to the outside of liposomes in a manner that is dependent on ATPase activity
GO:0016020 membrane
IEA
GO_REF:0000002
ACCEPT
Summary: membrane accurately describes the membrane-embedded ABCD4 cobalamin transporter.
Reason: Purified ABCD4 reconstituted in liposomes catalyzes ATP-dependent cobalamin translocation (PMID:33845046); localization experiments establish ER and lysosomal membranes (PMID:27456980). The broad transporter, transport and membrane terms are true core properties alongside the more specific vitamin-B12 transporter annotation. Greater specificity does not make these existing parent-level assertions over-annotations.
Supporting Evidence:
PMID:33845046
ABCD4 transports cobalamin from the inside to the outside of liposomes in a manner that is dependent on ATPase activity
GO:0016887 ATP hydrolysis activity
IEA
GO_REF:0000002
ACCEPT
Summary: ATP hydrolysis activity from InterPro ABC ATP-binding domain signatures. Directly supported by ATPase assays on purified, reconstituted ABCD4.
Reason: Reconstituted ABCD4 exhibits ATPase activity that is stimulated by luminal cobalamin and abolished by the Walker A K427A mutation, confirming ATP hydrolysis as an intrinsic activity coupled to transport.
Supporting Evidence:
PMID:33845046
the cobalamin inside liposomes is recognized by ABCD4 as substrate and stimulates the ATP hydrolysis of ABCD4
GO:0055085 transmembrane transport
IEA
GO_REF:0000002
ACCEPT
Summary: transmembrane transport accurately describes the membrane-embedded ABCD4 cobalamin transporter.
Reason: Purified ABCD4 reconstituted in liposomes catalyzes ATP-dependent cobalamin translocation (PMID:33845046); localization experiments establish ER and lysosomal membranes (PMID:27456980). The broad transporter, transport and membrane terms are true core properties alongside the more specific vitamin-B12 transporter annotation. Greater specificity does not make these existing parent-level assertions over-annotations.
Supporting Evidence:
PMID:33845046
ABCD4 transports cobalamin from the inside to the outside of liposomes in a manner that is dependent on ATPase activity
GO:0140359 ABC-type transporter activity
IEA
GO_REF:0000002
ACCEPT
Summary: ABC-type transporter activity accurately describes the membrane-embedded ABCD4 cobalamin transporter.
Reason: Purified ABCD4 reconstituted in liposomes catalyzes ATP-dependent cobalamin translocation (PMID:33845046); localization experiments establish ER and lysosomal membranes (PMID:27456980). The broad transporter, transport and membrane terms are true core properties alongside the more specific vitamin-B12 transporter annotation. Greater specificity does not make these existing parent-level assertions over-annotations.
Supporting Evidence:
PMID:33845046
ABCD4 transports cobalamin from the inside to the outside of liposomes in a manner that is dependent on ATPase activity
GO:0005515 protein binding
IPI
PMID:27456980
Translocation of the ABC transporter ABCD4 from the endoplas...
REMOVE
Summary: IPI capturing the ABCD4-LMBD1 (LMBRD1, Q9NUN5) interaction. This is a functionally important interaction (LMBD1 escorts ABCD4 from the ER to the lysosome), but the bare "protein binding" term is uninformative.
Reason: The generic protein binding label does not specify a separate molecular function. Retain the interaction observations, including the functional LMBD1 escort interaction where relevant, but remove this uninformative term without claiming that the physical interaction is false or inventing a new binding function.
Supporting Evidence:
PMID:27456980
this translocation depends on the lysosomal targeting ability of
GO:0005515 protein binding
IPI
PMID:28514442
Architecture of the human interactome defines protein commun...
REMOVE
Summary: Bare "protein binding" IPI from a proteome-scale interactome screen (BioPlex) capturing the FAM234B (A2RU67) interaction.
Reason: The generic protein binding label does not specify a separate molecular function. Retain the interaction observations, including the functional LMBD1 escort interaction where relevant, but remove this uninformative term without claiming that the physical interaction is false or inventing a new binding function.
Supporting Evidence:
PMID:28514442
Architecture of the human interactome defines protein communities and disease networks.
GO:0005515 protein binding
IPI
PMID:28572511
Clinical or ATPase domain mutations in ABCD4 disrupt the int...
REMOVE
Summary: IPI capturing the ABCD4-LMBD1 interaction demonstrated by a live-cell FRET assay. Functionally important but the bare term is uninformative.
Reason: The generic protein binding label does not specify a separate molecular function. Retain the interaction observations, including the functional LMBD1 escort interaction where relevant, but remove this uninformative term without claiming that the physical interaction is false or inventing a new binding function.
Supporting Evidence:
PMID:28572511
we demonstrated selective
GO:0005515 protein binding
IPI
PMID:33961781
Dual proteome-scale networks reveal cell-specific remodeling...
REMOVE
Summary: Bare "protein binding" IPI from a proteome-scale interactome screen (BioPlex 3.0) capturing the FAM234B (A2RU67) interaction.
Reason: The generic protein binding label does not specify a separate molecular function. Retain the interaction observations, including the functional LMBD1 escort interaction where relevant, but remove this uninformative term without claiming that the physical interaction is false or inventing a new binding function.
Supporting Evidence:
PMID:33961781
Dual proteome-scale networks reveal cell-specific remodeling of the human interactome.
GO:0042802 identical protein binding
IPI
PMID:27456980
Translocation of the ABC transporter ABCD4 from the endoplas...
KEEP AS NON CORE
Summary: Self-interaction (homodimerization) of ABCD4, consistent with its function as a half-size ABC transporter that operates as a homodimer.
Reason: ABCD4 is a half-transporter that assembles into a homodimer to form the functional unit, so identical protein binding is genuine and biologically meaningful, but it is a structural/assembly property rather than the core catalytic function.
Supporting Evidence:
PMID:27456980
consistent in mass with dimeric ABCD4
GO:0042802 identical protein binding
IPI
PMID:40205054
Multimodal cell maps as a foundation for structural and func...
KEEP AS NON CORE
Summary: Self-interaction of ABCD4 detected in a multimodal cell-mapping/interactome study, consistent with homodimer assembly.
Reason: Supports the homodimeric assembly of ABCD4; genuine but a structural property rather than the core transport function.
Supporting Evidence:
PMID:40205054
Multimodal cell maps as a foundation for structural and functional genomics.
GO:0015889 cobalamin transport
TAS
Reactome:R-HSA-9758881
ACCEPT
Summary: Reactome-asserted involvement in cobalamin transport (dietary cobalamin uptake pathway). This is the core biological process of ABCD4.
Reason: Cobalamin transport across the lysosomal membrane is the established core role of ABCD4, independently supported by experimental transport and disease data.
Supporting Evidence:
PMID:33845046
ABCD4 plays a key role in the transport of cobalamin from the lysosomal lumen to the cytosol
GO:0015889 cobalamin transport
TAS
Reactome:R-HSA-9758890
ACCEPT
Summary: Reactome-asserted involvement in cobalamin transport (transport of RCbl within the body). Core biological process of ABCD4.
Reason: Duplicate assertion of the core cobalamin-transport role from a related Reactome pathway; well supported by experimental and clinical evidence.
Supporting Evidence:
PMID:33845046
ABCD4 plays a key role in the transport of cobalamin from the lysosomal lumen to the cytosol
GO:0015420 ABC-type vitamin B12 transporter activity
EXP
PMID:33845046
The lysosomal protein ABCD4 can transport vitamin B(12) acro...
ACCEPT
Summary: Direct in vitro demonstration that purified, reconstituted ABCD4 transports cobalamin across liposomal membranes in an ATP-dependent manner. This is the definitive core molecular function.
Reason: The strongest evidence for ABCD4's function - reconstituted ABCD4 transports cobalamin (Km 426 uM), the activity is ATPase-dependent, and the Walker A K427A mutant abolishes both ATPase and transport. Defines the exact core MF.
Supporting Evidence:
PMID:33845046
ABCD4 transports cobalamin from the inside to the outside of liposomes in a manner that is dependent on ATPase activity
GO:0005765 lysosomal membrane
EXP
PMID:22922874
Mutations in ABCD4 cause a new inborn error of vitamin B12 m...
ACCEPT
Summary: Experimental demonstration that ABCD4 colocalizes with the lysosomal markers LAMP1 and LMBD1, establishing lysosomal membrane localization.
Reason: Directly supported experimental localization to the lysosomal membrane, the functional site of ABCD4's cobalamin-export activity.
Supporting Evidence:
PMID:22922874
in failure to release vitamin B12 from lysosomes, which mimics the cblF defect
GO:0005765 lysosomal membrane
EXP
PMID:25535791
Purification and interaction analyses of two human lysosomal...
ACCEPT
Summary: Lysosomal vitamin B12 transporter localization from the ABCD4/LMBD1 purification and interaction study.
Reason: Consistent, well-supported lysosomal membrane localization; ABCD4 is one of the two lysosomal membrane B12 transporters characterized in this work.
Supporting Evidence:
PMID:25535791
Mutations in human LMBRD1 and ABCD4 prevent lysosomal export of vitamin B(12) to
GO:0005765 lysosomal membrane
EXP
PMID:28572511
Clinical or ATPase domain mutations in ABCD4 disrupt the int...
ACCEPT
Summary: Lysosomal targeting of ABCD4 (dependent on LMBD1 co-expression) shown by live-cell assays.
Reason: Experimental support for lysosomal membrane localization; the study also shows this localization depends on interaction with LMBD1.
Supporting Evidence:
PMID:28572511
targeting depends on co-expression of, and interaction with, LMBD1. These data
GO:0005765 lysosomal membrane
IDA
PMID:33845046
The lysosomal protein ABCD4 can transport vitamin B(12) acro...
ACCEPT
Summary: ABCD4 is active (transports cobalamin) at the lysosomal membrane, its physiological site of action.
Reason: The lysosomal membrane is where ABCD4 performs its cobalamin-export function; is_active_in is appropriate given the demonstrated transport activity and lysosomal localization.
Supporting Evidence:
PMID:33845046
ABCD4 is located on lysosomal membrane
GO:0009235 cobalamin metabolic process
IDA
PMID:33845046
The lysosomal protein ABCD4 can transport vitamin B(12) acro...
ACCEPT
Summary: ABCD4 participates in cobalamin metabolism by exporting lysosomal cobalamin to the cytosol for cofactor synthesis.
Reason: By delivering cobalamin to the cytosol for conversion to methylcobalamin and adenosylcobalamin, ABCD4 is a core component of intracellular cobalamin metabolism; directly supported.
Supporting Evidence:
PMID:33845046
cobalamin is released into the cytosol and converted into two active cofactors: methylcobalamin and adenosylcobalamin
GO:0015420 ABC-type vitamin B12 transporter activity
IDA
PMID:33845046
The lysosomal protein ABCD4 can transport vitamin B(12) acro...
ACCEPT
Summary: Direct-assay support (IDA) for the ABC-type vitamin B12 transporter activity of ABCD4. Core molecular function.
Reason: Same definitive in vitro transport evidence; the exact GOA MF term for ABCD4's core function.
Supporting Evidence:
PMID:33845046
ABCD4 transports cobalamin from the inside to the outside of liposomes in a manner that is dependent on ATPase activity
GO:0005765 lysosomal membrane
IDA
PMID:33845046
The lysosomal protein ABCD4 can transport vitamin B(12) acro...
ACCEPT
Summary: Direct-assay lysosomal membrane localization of ABCD4.
Reason: Consistent with all other experimental evidence for lysosomal membrane localization.
Supporting Evidence:
PMID:33845046
ABCD4 is located on lysosomal membrane
GO:0005515 protein binding
IPI
PMID:33845046
The lysosomal protein ABCD4 can transport vitamin B(12) acro...
REMOVE
Summary: IPI capturing the ABCD4-LMBD1 (Q9NUN5) interaction from the in vitro pull-down/crosslinking analyses. Functionally central but the bare term is uninformative.
Reason: The generic protein binding label does not specify a separate molecular function. Retain the interaction observations, including the functional LMBD1 escort interaction where relevant, but remove this uninformative term without claiming that the physical interaction is false or inventing a new binding function.
Supporting Evidence:
PMID:33845046
purified ABCD4 and LMBD1 interact each other with a 1:1 stoichiometry
GO:0015420 ABC-type vitamin B12 transporter activity
IMP
PMID:33845046
The lysosomal protein ABCD4 can transport vitamin B(12) acro...
ACCEPT
Summary: Mutant-phenotype support (IMP) for the ABC-type vitamin B12 transporter activity - disease and engineered mutations abolish cobalamin transport.
Reason: Loss-of-function mutations (e.g. Walker A K427A, clinical Y319C) abolish cobalamin transport, providing mutant-phenotype evidence for this core molecular function.
Supporting Evidence:
PMID:33845046
ABCD4 (K427A) had lost transport activity in addition to ATPase activity
GO:0015889 cobalamin transport
IMP
PMID:33845046
The lysosomal protein ABCD4 can transport vitamin B(12) acro...
ACCEPT
Summary: Mutant-phenotype support for ABCD4's role in cobalamin transport. Core biological process.
Reason: Mutations that impair ABCD4 abolish cobalamin transport across the lysosomal membrane, directly implicating ABCD4 in this process.
Supporting Evidence:
PMID:33845046
ABCD4 plays a key role in the transport of cobalamin from the lysosomal lumen to the cytosol
GO:0005765 lysosomal membrane
IDA
PMID:27456980
Translocation of the ABC transporter ABCD4 from the endoplas...
ACCEPT
Summary: Direct-assay lysosomal membrane localization; ABCD4 localizes to lysosomes upon LMBD1-mediated translocation from the ER.
Reason: Well-supported experimental localization; the study establishes that lysosomal localization is achieved via LMBD1-dependent translocation.
Supporting Evidence:
PMID:27456980
this translocation depends on the lysosomal targeting ability of
GO:0005789 endoplasmic reticulum membrane
IDA
PMID:27456980
Translocation of the ABC transporter ABCD4 from the endoplas...
ACCEPT
Summary: Direct-assay ER membrane localization; ABCD4 is an ER-resident protein before LMBD1-dependent lysosomal targeting.
Reason: Experimentally demonstrated ER localization (biosynthetic-intermediate site); endogenous ABCD4 distributes between ER and lysosome, with LMBD1 controlling the lysosomal fraction.
Supporting Evidence:
PMID:27456980
ABCD4 was not a peroxisomal protein, but rather, an ER protein
GO:0005515 protein binding
IPI
PMID:25535791
Purification and interaction analyses of two human lysosomal...
REMOVE
Summary: IPI capturing the ABCD4 interactions with LMBD1 (Q9NUN5) and MMACHC (Q9Y4U1) from SPR/biophysical analyses. Both are functionally central (lysosomal cobalamin-to-cytosol trafficking complex), but the bare term is uninformative.
Reason: The generic protein binding label does not specify a separate molecular function. Retain the interaction observations, including the functional LMBD1 escort interaction where relevant, but remove this uninformative term without claiming that the physical interaction is false or inventing a new binding function.
Supporting Evidence:
PMID:25535791
LMBD1 and ABCD4 interact with low
PMID:25535791
MMACHC also interacts with LMBD1 and ABCD4 with low nanomolar affinity.
GO:0005777 peroxisome
IDA NOT
PMID:19010322
70-kDa peroxisomal membrane protein related protein (P70R/AB...
ACCEPT
Summary: NOT annotation - ABCD4 does NOT localize to peroxisomes. This study showed P70R/ABCD4 localizes to the ER, not peroxisomes.
Reason: Correct negative annotation directly supported by the primary data overturning the original peroxisomal assignment.
Supporting Evidence:
PMID:19010322
reticulum (ER), not to peroxisomes.
GO:0005777 peroxisome
IDA NOT
PMID:27456980
Translocation of the ABC transporter ABCD4 from the endoplas...
ACCEPT
Summary: NOT annotation - ABCD4 does NOT localize to peroxisomes; it is an ER/lysosomal protein.
Reason: Correct negative annotation; the study explicitly shows ABCD4 is not a peroxisomal protein.
Supporting Evidence:
PMID:27456980
ABCD4 was not a peroxisomal protein, but rather, an ER protein
GO:0005777 peroxisome
IDA
PMID:14533738
Targeting of the human adrenoleukodystrophy protein to the p...
UNDECIDED
Summary: The 2003 paper reports peroxisomal targeting of GFP-labelled ABCD4 fragments, whereas later work places full-length ABCD4 in ER and lysosomes.
Reason: PMID:14533738 explicitly includes human PMP69 fragments; it must not be dismissed because its title foregrounds ABCD1. Fragment targeting can coexist with full-length targeting determined by the N terminus, so the later negative localization assays do not by themselves falsify the reported construct result. The cached source is abstract-only; reconciliation requires the exact ABCD4 construct and localization evidence before deciding how that experimental observation should annotate the intact gene product.
Supporting Evidence:
PMID:14533738
Green fluorescent protein-labeled fragments of human peroxisomal membrane protein 69
GO:0005777 peroxisome
IDA
PMID:9302272
Identification of a fourth half ABC transporter in the human...
REMOVE
Summary: The early peroxisomal assignment is contradicted for intact human ABCD4 by later direct targeting and localization experiments.
Reason: This is not a claim that the original paper assayed the wrong gene. PMID:27456980 explicitly revisits the older antibody-based rat hepatic peroxisome result and contrasts it with human ABCD4 expression/localization, then establishes endogenous ER/lysosome pools. Together with the targeting experiments in PMID:19010322, this supports withdrawing the general native-human peroxisome assignment. Species, antibody and construct context remain limitations of reconciling the historical experiment, whose full text is unavailable here.
Supporting Evidence:
PMID:27456980
ABCD4 does not localize to peroxisomes
PMID:19010322
only P70R lacks the region and is translated with NH(2)-terminal hydrophobic TMS1.
GO:0005765 lysosomal membrane
TAS
Reactome:R-HSA-5683325
ACCEPT
Summary: Reactome-asserted lysosomal membrane localization (defective-transport event). Consistent with all experimental localization data.
Reason: Correct lysosomal membrane localization, agreeing with the direct experimental evidence.
Supporting Evidence:
PMID:22922874
in failure to release vitamin B12 from lysosomes, which mimics the cblF defect
GO:0005765 lysosomal membrane
TAS
Reactome:R-HSA-5223313
ACCEPT
Summary: Reactome-asserted lysosomal membrane localization (RCbl transport in gut mucosal cells). Consistent with experimental data.
Reason: Correct lysosomal membrane localization.
Supporting Evidence:
PMID:33845046
ABCD4 is located on lysosomal membrane
GO:0005765 lysosomal membrane
TAS
Reactome:R-HSA-9759206
ACCEPT
Summary: Reactome-asserted lysosomal membrane localization (ABCD4-LMBRD1 transports RCbl from lysosomal lumen to cytosol). Consistent with experimental data.
Reason: Correct lysosomal membrane localization, matching the functional ABCD4-LMBRD1 export event.
Supporting Evidence:
PMID:33845046
ABCD4 is located on lysosomal membrane
GO:0009235 cobalamin metabolic process
IMP
PMID:22922874
Mutations in ABCD4 cause a new inborn error of vitamin B12 m...
ACCEPT
Summary: Mutant-phenotype support for ABCD4's role in cobalamin metabolism - mutations cause a new inborn error of vitamin B12 metabolism (cblJ).
Reason: ABCD4 mutations cause failure to release cobalamin from lysosomes and impaired cofactor synthesis, directly implicating ABCD4 in cobalamin metabolism.
Supporting Evidence:
PMID:22922874
the ATPase activity of ABCD4 may
GO:0005524 ATP binding
NAS
PMID:9266848
Primary structure of human PMP69, a putative peroxisomal ABC...
ACCEPT
Summary: Author statement of ATP binding based on the ABC-half-transporter sequence identification. Consistent with the experimentally confirmed nucleotide-binding domain.
Reason: ATP binding is supported by the canonical ABC nucleotide-binding domain and by subsequent ATPase-dependent transport assays; the NAS assertion is correct.
Supporting Evidence:
PMID:9266848
ABC-half-transporters require a partner
GO:0016020 membrane
NAS
PMID:9266848
Primary structure of human PMP69, a putative peroxisomal ABC...
ACCEPT
Summary: membrane accurately describes the membrane-embedded ABCD4 cobalamin transporter.
Reason: Purified ABCD4 reconstituted in liposomes catalyzes ATP-dependent cobalamin translocation (PMID:33845046); localization experiments establish ER and lysosomal membranes (PMID:27456980). The broad transporter, transport and membrane terms are true core properties alongside the more specific vitamin-B12 transporter annotation. Greater specificity does not make these existing parent-level assertions over-annotations.
Supporting Evidence:
PMID:33845046
ABCD4 transports cobalamin from the inside to the outside of liposomes in a manner that is dependent on ATPase activity
GO:0042626 ATPase-coupled transmembrane transporter activity
NAS
PMID:9266848
Primary structure of human PMP69, a putative peroxisomal ABC...
ACCEPT
Summary: ATPase-coupled transmembrane transporter activity accurately describes the membrane-embedded ABCD4 cobalamin transporter.
Reason: Purified ABCD4 reconstituted in liposomes catalyzes ATP-dependent cobalamin translocation (PMID:33845046); localization experiments establish ER and lysosomal membranes (PMID:27456980). The broad transporter, transport and membrane terms are true core properties alongside the more specific vitamin-B12 transporter annotation. Greater specificity does not make these existing parent-level assertions over-annotations.
Supporting Evidence:
PMID:33845046
ABCD4 transports cobalamin from the inside to the outside of liposomes in a manner that is dependent on ATPase activity
GO:0043190 ATP-binding cassette (ABC) transporter complex
NAS
PMID:9266848
Primary structure of human PMP69, a putative peroxisomal ABC...
ACCEPT
Summary: Author statement that ABCD4 is part of an ABC transporter complex. ABCD4 is a half-transporter that functions as a homodimer (and associates with LMBD1), so it is part of an ABC transporter complex.
Reason: As a half-size ABC transporter, ABCD4 assembles into a homodimeric functional complex, consistent with this cellular-component annotation.
Supporting Evidence:
PMID:9266848
ABC-half-transporter to constitute a functional complex, either as a homodimer
GO:0055085 transmembrane transport
NAS
PMID:9266848
Primary structure of human PMP69, a putative peroxisomal ABC...
ACCEPT
Summary: transmembrane transport accurately describes the membrane-embedded ABCD4 cobalamin transporter.
Reason: Purified ABCD4 reconstituted in liposomes catalyzes ATP-dependent cobalamin translocation (PMID:33845046); localization experiments establish ER and lysosomal membranes (PMID:27456980). The broad transporter, transport and membrane terms are true core properties alongside the more specific vitamin-B12 transporter annotation. Greater specificity does not make these existing parent-level assertions over-annotations.
Supporting Evidence:
PMID:33845046
ABCD4 transports cobalamin from the inside to the outside of liposomes in a manner that is dependent on ATPase activity

Core Functions

ATP-dependent lysosomal cobalamin (vitamin B12) exporter that hydrolyzes ATP to translocate cobalamin from the lysosomal lumen to the cytosol, functioning as a homodimer at the lysosomal membrane.

Supporting Evidence:
  • PMID:33845046
    ABCD4 transports cobalamin from the inside to the outside of liposomes in a manner that is dependent on ATPase activity
  • file:human/ABCD4/ABCD4-uniprot.txt
    from the lysosomal lumen to the cytosol in an ATP-dependent manner

Intrinsic ATPase / nucleotide-binding activity of the ABC transporter nucleotide-binding domain that energizes cobalamin transport; ATP binding and hydrolysis are coupled to substrate translocation (Walker A K427 is essential).

Molecular Function:
ATP hydrolysis activity
Directly Involved In:
Cellular Locations:
Supporting Evidence:
  • PMID:33845046
    the cobalamin inside liposomes is recognized by ABCD4 as substrate and stimulates the ATP hydrolysis of ABCD4

References

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Deep Research

OpenScientist

(ABCD4-hypotheses/fatty-acid-functions-and-peroxisome-organization/openscientist.md)

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📚 Additional Documentation

Notes

(ABCD4-notes.md)

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