UFC1

UniProt ID: Q9Y3C8
Organism: Homo sapiens
Review Status: COMPLETE
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Gene Description

UFC1 (Ubiquitin-fold modifier-conjugating enzyme 1) is the E2-like conjugating enzyme of the UFM1 (ufmylation) cascade, a ubiquitin-like protein-conjugation system that proceeds through E1 (UBA5), E2 (UFC1) and E3 (UFL1/DDRGK1/CDK5RAP3) enzymes. UFC1 accepts the activated ubiquitin-fold modifier UFM1 from the E1 enzyme UBA5 and forms a thioester-linked intermediate at its catalytic cysteine (Cys-116), then, in concert with the UFL1-DDRGK1 E3 ligase, transfers UFM1 onto substrate lysines. The principal physiological substrate is the 60S ribosomal protein RPL26/uL24 on endoplasmic-reticulum-bound ribosomes, where ufmylation promotes recycling of post-termination or stalled 60S subunits from SEC61 translocons and supports ribosome-associated quality control. UFMylation more broadly participates in the response to ER stress, reticulophagy (ER-phagy), DNA-damage signaling and innate-immune/interferon signaling. UFC1 is a small (167 aa) cytosolic protein structurally related to ubiquitin-conjugating (E2) enzymes; biallelic loss-of-function variants cause a neurodevelopmental disorder with spasticity and poor growth, underscoring an essential role of ufmylation in brain development.

Existing Annotations Review

GO Term Evidence Action Reason
GO:0005737 cytoplasm
IBA
GO_REF:0000033
ACCEPT
Summary: UFC1 is a small soluble protein that acts in the cytoplasm/cytosol, where it receives UFM1 from UBA5 and works with the ER-membrane-anchored UFL1/DDRGK1 E3 to ufmylate ER-bound ribosomes.
Reason: Cytoplasmic site of action is consistent with the biochemistry of the cascade; UFC1 is a cytosolic E2 that delivers UFM1 to the membrane-tethered E3 complex.
Supporting Evidence:
file:human/UFC1/UFC1-goa.tsv
UFC1 is_active_in GO:0005737 cytoplasm
GO:0071568 UFM1 transferase activity
IBA
GO_REF:0000033
ACCEPT
Summary: UFM1 transferase activity is a near-synonymous parent of the specific E2 UFM1-conjugating activity of UFC1; it captures the same core molecular function (transfer of UFM1).
Reason: UFC1 catalyzes transfer of UFM1 from a thioester intermediate to substrate; this MF term correctly describes that activity, though GO:0061657 (UFM1 conjugating enzyme activity) is the most precise E2-step term.
Supporting Evidence:
file:human/UFC1/UFC1-uniprot.txt
E2-like enzyme which specifically catalyzes the second step in ufmylation
GO:0034976 response to endoplasmic reticulum stress
IBA
GO_REF:0000033
KEEP AS NON CORE
Summary: Ufmylation, in which UFC1 is the E2, is induced by and functions in the response to ER stress, linking the modification of ER-bound ribosomes to ER homeostasis.
Reason: This is a downstream biological process that UFC1 participates in via its catalytic role; it is a valid pathway context but non-core relative to the E2 conjugating activity.
Supporting Evidence:
file:human/UFC1/UFC1-uniprot.txt
Ufmylation is involved in various processes, such as ribosome recycling, response to DNA damage, interferon response or reticulophagy
GO:0061709 reticulophagy
IBA
GO_REF:0000033
KEEP AS NON CORE
Summary: UFC1, as the cascade E2, contributes to reticulophagy (ER-phagy) driven by ER-resident ufmylation.
Reason: Reticulophagy is a downstream process of ER ufmylation; a valid but non-core process annotation for the E2 enzyme.
Supporting Evidence:
file:human/UFC1/UFC1-uniprot.txt
Ufmylation is involved in various processes, such as ribosome recycling, response to DNA damage, interferon response or reticulophagy
GO:0061657 UFM1 conjugating enzyme activity
IEA
GO_REF:0000120
ACCEPT
Summary: This is the precise E2 molecular function of UFC1 - it forms a thioester intermediate with UFM1 and conjugates it to substrate. Multiple direct experimental annotations corroborate this electronic one.
Reason: UFM1 conjugating enzyme (E2) activity is the core molecular function of UFC1, supported by founding biochemistry and structures.
Supporting Evidence:
file:human/UFC1/UFC1-uniprot.txt
Accepts the ubiquitin-like modifier UFM1 from the E1 enzyme UBA5 and forms an intermediate with UFM1 via a thioester linkage
GO:0071569 protein ufmylation
IEA
GO_REF:0000120
ACCEPT
Summary: Protein ufmylation is the biological process that the UFC1 E2 step belongs to.
Reason: UFC1 is an essential catalytic component of ufmylation; the process annotation is well supported.
Supporting Evidence:
file:human/UFC1/UFC1-uniprot.txt
E2-like enzyme which specifically catalyzes the second step in ufmylation
GO:0005515 protein binding
IPI
PMID:25902260
Autism and intellectual disability-associated KIRREL3 intera...
KEEP AS NON CORE
Summary: IntAct interaction with KIRREL3 (Q8IZU9) from an autism/intellectual-disability interactome screen. Bare protein binding is uninformative and this partner is not part of the ufmylation cascade.
Reason: Bare protein binding from a single screen with a non-cascade partner does not inform UFC1's core E2 function.
Supporting Evidence:
file:human/UFC1/UFC1-goa.tsv
GO:0005515 protein binding molecular_function ECO:0000353 IPI PMID:25902260 UniProtKB:Q8IZU9
GO:0005515 protein binding
IPI
PMID:32296183
A reference map of the human binary protein interactome.
KEEP AS NON CORE
Summary: Binary interactome (HuRI) interactions. Bare protein binding is uninformative.
Reason: Records real high-throughput interactions but the term itself is uninformative; the core MF is captured by UFM1 conjugating enzyme activity.
Supporting Evidence:
file:human/UFC1/UFC1-goa.tsv
GO:0005515 protein binding molecular_function ECO:0000353 IPI PMID:32296183 UniProtKB:P57678
GO:0005515 protein binding
IPI
PMID:32814053
Interactome Mapping Provides a Network of Neurodegenerative ...
KEEP AS NON CORE
Summary: Neurodegeneration interactome screen interaction. Bare protein binding is uninformative and the partner is not part of the cascade.
Reason: Single high-throughput interaction unrelated to UFC1's catalytic function.
Supporting Evidence:
file:human/UFC1/UFC1-goa.tsv
GO:0005515 protein binding molecular_function ECO:0000353 IPI PMID:32814053 UniProtKB:O60260-5
GO:0005515 protein binding
IPI
PMID:33961781
Dual proteome-scale networks reveal cell-specific remodeling...
KEEP AS NON CORE
Summary: BioPlex affinity-purification interaction with UFL1 (O94874), the cognate E3 ligase. This is a genuine cascade interaction, but the bare term is uninformative.
Reason: The WITH partner is UFL1, a bona fide cascade partner; the interaction is real but the generic term is non-core. The informative MF is the E2 activity.
Supporting Evidence:
file:human/UFC1/UFC1-goa.tsv
GO:0005515 protein binding molecular_function ECO:0000353 IPI PMID:33961781 UniProtKB:O94874
GO:0005515 protein binding
IPI
PMID:37595036
Mechanistic insights into the roles of the UFM1 E3 ligase co...
KEEP AS NON CORE
Summary: Interaction with UFL1 (O94874) reported in the mechanistic study of the UFM1 E3 ligase complex. Genuine cascade interaction; bare term is uninformative.
Reason: Partner is a core UREL-complex component; real but non-core under the generic term.
Supporting Evidence:
file:human/UFC1/UFC1-goa.tsv
GO:0005515 protein binding molecular_function ECO:0000353 IPI PMID:37595036 UniProtKB:O94874
GO:0005515 protein binding
IPI
PMID:40205054
Multimodal cell maps as a foundation for structural and func...
KEEP AS NON CORE
Summary: Multimodal cell-maps interaction with CDK5RAP3 (Q96JB5), a UREL-complex component. Bare protein binding is uninformative.
Reason: Real interaction with a cascade-associated protein; non-core under generic term.
Supporting Evidence:
file:human/UFC1/UFC1-goa.tsv
GO:0005515 protein binding molecular_function ECO:0000353 IPI PMID:40205054 UniProtKB:Q96JB5
GO:0032649 regulation of type II interferon production
IEA
GO_REF:0000107
KEEP AS NON CORE
Summary: Inferred from the mouse ortholog; ufmylation regulates innate-immune/interferon signaling, but a specific causal role of UFC1 in type II interferon production in human is not directly demonstrated here.
Reason: Plausible electronic transfer reflecting ufmylation's role in immune signaling; peripheral to UFC1's catalytic function.
Supporting Evidence:
file:human/UFC1/UFC1-uniprot.txt
interferon response
GO:0032649 regulation of type II interferon production
ISS
GO_REF:0000024
KEEP AS NON CORE
Summary: Sequence-similarity transfer from the mouse ortholog for the same immune-signaling role.
Reason: Same rationale as the IEA annotation; non-core, plausible by orthology.
Supporting Evidence:
file:human/UFC1/UFC1-uniprot.txt
interferon response
GO:0061657 UFM1 conjugating enzyme activity
IDA
PMID:34588452
Structural basis for UFM1 transfer from UBA5 to UFC1.
ACCEPT
Summary: Structural/biochemical demonstration of UFM1 transfer from UBA5 to UFC1, establishing UFC1's E2 conjugating activity directly.
Reason: Direct experimental evidence for the core E2 function; structures show activation of the UFC1 active site upon UBA5 binding.
Supporting Evidence:
file:human/UFC1/UFC1-uniprot.txt
Accepts the ubiquitin-like modifier UFM1 from the E1 enzyme UBA5 and forms an intermediate with UFM1 via a thioester linkage
GO:0071569 protein ufmylation
IDA
PMID:34588452
Structural basis for UFM1 transfer from UBA5 to UFC1.
ACCEPT
Summary: Direct evidence that UFC1 participates in ufmylation via UFM1 transfer.
Reason: Well-supported process annotation for the cascade E2.
Supporting Evidence:
file:human/UFC1/UFC1-uniprot.txt
E2-like enzyme which specifically catalyzes the second step in ufmylation
GO:0061657 UFM1 conjugating enzyme activity
IMP
PMID:37036982
RPL26/uL24 UFMylation is essential for ribosome-associated q...
ACCEPT
Summary: Functional (mutant/knockout) evidence that UFC1 conjugating activity is required for RPL26/uL24 ufmylation and ER ribosome-associated quality control.
Reason: Direct functional support for the core E2 activity in the physiological RQC context.
Supporting Evidence:
PMID:37036982
RQC-dependent degradation of ER-APs strictly requires conjugation of the
GO:0071569 protein ufmylation
IMP
PMID:37036982
RPL26/uL24 UFMylation is essential for ribosome-associated q...
ACCEPT
Summary: UFC1 is required for ufmylation of 60S ribosomes at the ER, supporting the process annotation.
Reason: Functional evidence ties UFC1 to ER ribosome ufmylation.
Supporting Evidence:
PMID:37036982
UFMylation of translocon-bound 60S subunits modulates the RTJ
GO:0061657 UFM1 conjugating enzyme activity
IDA
PMID:36121123
A non-canonical scaffold-type E3 ligase complex mediates pro...
ACCEPT
Summary: Demonstration that the UFL1/DDRGK1 scaffold-type E3 activates UFC1 for aminolysis (UFM1 transfer); UFC1 Lys-108 is required.
Reason: Direct biochemical support for the E2 conjugating activity within the non-canonical E2-E3 mechanism.
Supporting Evidence:
file:human/UFC1/UFC1-goa.tsv
GO:0061657 UFM1 conjugating enzyme activity molecular_function ECO:0000314 IDA PMID:36121123
GO:0061657 UFM1 conjugating enzyme activity
IDA
PMID:38383789
The UFM1 E3 ligase recognizes and releases 60S ribosomes fro...
ACCEPT
Summary: Structures of the UFC1-UFL1-UFM1-DDRGK1 complex and ribosome ufmylation assays establish UFC1's conjugating activity in the context of 60S recycling.
Reason: Direct structural and functional support for the core E2 activity.
Supporting Evidence:
PMID:38383789
the ubiquitin-like protein UFM1 on the 60S ribosomal subunit protein RPL26
GO:0071569 protein ufmylation
IMP
PMID:30626644
Ribosomal protein RPL26 is the principal target of UFMylatio...
ACCEPT
Summary: UFC1 is required for ufmylation; RPL26 identified as the principal target.
Reason: Functional support for UFC1's role in ufmylation.
Supporting Evidence:
PMID:30626644
Ribosomal protein RPL26 is the principal target of UFMylation
GO:0071569 protein ufmylation
IDA
PMID:36121123
A non-canonical scaffold-type E3 ligase complex mediates pro...
ACCEPT
Summary: Direct evidence that UFC1, activated by the scaffold E3, ufmylates substrate.
Reason: Supports the process annotation for the E2.
Supporting Evidence:
file:human/UFC1/UFC1-goa.tsv
GO:0071569 protein ufmylation biological_process ECO:0000314 IDA PMID:36121123
GO:0071569 protein ufmylation
IDA
PMID:38383789
The UFM1 E3 ligase recognizes and releases 60S ribosomes fro...
ACCEPT
Summary: Direct evidence for UFC1-dependent ufmylation of 60S ribosomes.
Reason: Supports the process annotation.
Supporting Evidence:
file:human/UFC1/UFC1-goa.tsv
GO:0071569 protein ufmylation biological_process ECO:0000314 IDA PMID:38383789
GO:0034976 response to endoplasmic reticulum stress
IMP
PMID:32160526
A genome-wide ER-phagy screen highlights key roles of mitoch...
KEEP AS NON CORE
Summary: Genome-wide ER-phagy screen implicating ER-resident ufmylation (including the E2 step) in ER stress responses.
Reason: Valid downstream process; non-core relative to the E2 catalytic activity.
Supporting Evidence:
file:human/UFC1/UFC1-uniprot.txt
response to DNA damage, interferon response or reticulophagy
GO:0061709 reticulophagy
IMP
PMID:32160526
A genome-wide ER-phagy screen highlights key roles of mitoch...
KEEP AS NON CORE
Summary: ER-phagy screen implicating the ufmylation pathway (UFC1 E2 step) in reticulophagy.
Reason: Valid downstream process; non-core.
Supporting Evidence:
file:human/UFC1/UFC1-uniprot.txt
reticulophagy
GO:0071569 protein ufmylation
IMP
PMID:32160526
A genome-wide ER-phagy screen highlights key roles of mitoch...
ACCEPT
Summary: ER-phagy screen confirms UFC1 involvement in ufmylation.
Reason: Supports the process annotation.
Supporting Evidence:
file:human/UFC1/UFC1-uniprot.txt
E2-like enzyme which specifically catalyzes the second step in ufmylation
GO:0005515 protein binding
IPI
PMID:30886146
UFL1 promotes histone H4 ufmylation and ATM activation.
KEEP AS NON CORE
Summary: Interaction with UFL1 (O94874) reported in the histone H4 ufmylation/ATM study. Genuine cascade partner; bare term uninformative.
Reason: Real interaction with the cognate E3; non-core under generic term.
Supporting Evidence:
file:human/UFC1/UFC1-goa.tsv
GO:0005515 protein binding molecular_function ECO:0000353 IPI PMID:30886146 UniProtKB:O94874
GO:0061657 UFM1 conjugating enzyme activity
IDA
PMID:15071506
A novel protein-conjugating system for Ufm1, a ubiquitin-fol...
ACCEPT
Summary: Founding paper identifying UFC1 as the E2 that accepts activated UFM1 from UBA5 via thioester linkage; defines the catalytic Cys.
Reason: Original direct demonstration of the core E2 UFM1-conjugating activity.
Supporting Evidence:
PMID:15071506
Activated Ufm1 is then transferred to its cognate
GO:0005515 protein binding
IPI
PMID:29868776
Biallelic UFM1 and UFC1 mutations expand the essential role ...
KEEP AS NON CORE
Summary: Interactions reported in the disease study (UFM1 P61960 among partners). Bare term uninformative, but reflects a cascade interaction.
Reason: Real cascade interaction (UFM1) but non-core under generic term.
Supporting Evidence:
file:human/UFC1/UFC1-goa.tsv
GO:0005515 protein binding molecular_function ECO:0000353 IPI PMID:29868776 UniProtKB:P61960
GO:0007420 brain development
IMP
PMID:29868776
Biallelic UFM1 and UFC1 mutations expand the essential role ...
KEEP AS NON CORE
Summary: Biallelic UFC1 variants (R23Q, T106I) that impair thioester formation and ufmylation cause a neurodevelopmental disorder, establishing an essential role of ufmylation in brain development.
Reason: A genuine, disease-supported physiological role, but a pleiotropic developmental outcome rather than UFC1's core molecular function.
Supporting Evidence:
file:human/UFC1/UFC1-uniprot.txt
Biallelic UFM1 and UFC1 mutations expand the essential role of ufmylation in brain development
GO:0071569 protein ufmylation
IMP
PMID:29868776
Biallelic UFM1 and UFC1 mutations expand the essential role ...
ACCEPT
Summary: Disease variants decrease ufmylation, functionally implicating UFC1 in the process.
Reason: Supports the process annotation with patient-variant evidence.
Supporting Evidence:
file:human/UFC1/UFC1-uniprot.txt
decreased protein ufmylation
GO:1990592 protein K69-linked ufmylation
IDA
PMID:25219498
Modification of ASC1 by UFM1 is crucial for ERΞ± transactivat...
KEEP AS NON CORE
Summary: UFC1 participates in UFM1 conjugation; UFM1 chains can be linked through Lys-69. This specific linkage-type process is part of ufmylation chemistry.
Reason: A specific sub-aspect of ufmylation (chain linkage type); valid but a narrow process annotation relative to the core E2 activity.
Supporting Evidence:
file:human/UFC1/UFC1-goa.tsv
GO:1990592 protein K69-linked ufmylation biological_process ECO:0000314 IDA PMID:25219498
GO:0070062 extracellular exosome
HDA
PMID:19056867
Large-scale proteomics and phosphoproteomics of urinary exos...
MARK AS OVER ANNOTATED
Summary: Detection of UFC1 in urinary exosome proteomics. This reflects proteomic presence rather than a functional extracellular localization.
Reason: High-throughput proteomic detection in exosomes does not reflect UFC1's cytosolic site of catalytic function.
Supporting Evidence:
file:human/UFC1/UFC1-goa.tsv
GO:0070062 extracellular exosome cellular_component ECO:0007005 HDA PMID:19056867
GO:0034976 response to endoplasmic reticulum stress
IDA
PMID:23152784
Transcriptional regulation of the Ufm1 conjugation system in...
KEEP AS NON CORE
Summary: The UFM1 conjugation system is transcriptionally up-regulated upon ER stress, consistent with a role in the ER stress response.
Reason: Valid pathway context; non-core relative to catalytic activity.
Supporting Evidence:
file:human/UFC1/UFC1-goa.tsv
GO:0034976 response to endoplasmic reticulum stress biological_process ECO:0000314 IDA PMID:23152784
GO:0071569 protein ufmylation
IMP
PMID:23152784
Transcriptional regulation of the Ufm1 conjugation system in...
ACCEPT
Summary: UFC1 is part of the UFM1 conjugation system implicated in this study.
Reason: Supports the process annotation.
Supporting Evidence:
file:human/UFC1/UFC1-goa.tsv
GO:0071569 protein ufmylation biological_process ECO:0000315 IMP PMID:23152784
GO:0005515 protein binding
IPI
PMID:20018847
A novel type of E3 ligase for the Ufm1 conjugation system.
KEEP AS NON CORE
Summary: Interaction with UFL1 (O94874) from the paper identifying the UFM1 E3 ligase. Genuine cascade interaction; bare term uninformative.
Reason: Real cascade interaction but non-core under generic term; the informative MF is the E2 activity.
Supporting Evidence:
file:human/UFC1/UFC1-goa.tsv
GO:0005515 protein binding molecular_function ECO:0000353 IPI PMID:20018847 UniProtKB:O94874
GO:0071569 protein ufmylation
IDA
PMID:15071506
A novel protein-conjugating system for Ufm1, a ubiquitin-fol...
ACCEPT
Summary: Founding biochemical demonstration of the UFM1 conjugation system in which UFC1 is the E2.
Reason: Direct evidence for the process; UFC1 is the cascade E2.
Supporting Evidence:
PMID:15071506
Activated Ufm1 is then transferred to its cognate

Core Functions

E2 UFM1-conjugating enzyme that accepts activated UFM1 from the E1 enzyme UBA5 via a thioester intermediate at its catalytic Cys-116 and, with the UFL1/DDRGK1 E3 ligase, transfers UFM1 onto substrate lysines (notably RPL26/uL24 on ER-bound 60S ribosomes).

Cellular Locations:
Supporting Evidence:
  • file:human/UFC1/UFC1-uniprot.txt
    Accepts the ubiquitin-like modifier UFM1 from the E1 enzyme UBA5 and forms an intermediate with UFM1 via a thioester linkage
  • PMID:15071506
    Activated Ufm1 is then transferred to its cognate

References

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Suggested Questions for Experts

Q: Beyond RPL26/uL24, what is the full physiological substrate repertoire of UFC1-dependent ufmylation, and which substrates are direct E2 products versus E3-determined?

Q: How do the disease variants R23Q and T106I mechanistically reduce thioester formation, and does residual activity correlate with phenotype severity?

Suggested Experiments

Experiment: Reconstitute the UBA5-UFC1-UFL1/DDRGK1 cascade in vitro with purified components and 60S ribosomes to quantify the kinetic contribution of UFC1 active-site activation to RPL26 ufmylation.

Experiment: CRISPR knock-in of UFC1 catalytic (C116S) or disease (R23Q/T106I) alleles in cells followed by ribosome-ufmylation and ER-RQC reporter assays to test the requirement of E2 activity for 60S recycling.

πŸ“š Additional Documentation

Notes

(UFC1-notes.md)

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Pn Notes

(UFC1-pn-notes.md)

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